| 300000041030 |
Adeno-associated virus serotype 5 vector encoding C1-esterase inhibitor
|
|
Current
|
| 300000052503 |
Adeno-associated virus serotype 8 containing the human LDLR gene
|
|
Current
|
| 300000000480 |
Adeno-associated virus serotype 8 containing the human RdCVF sequence and the human RdCVFL sequence
|
|
Current
|
| 300000040113 |
Adeno-associated virus serotype 8 expressing the human gamma-sarcoglycan gene
|
|
Current
|
| 100000183209 |
ADENO-ASSOCIATED VIRUS SEROTYPE 8 VECTOR CONTAINING THE HUMAN AIPL1 GENE
|
|
Current
|
| 300000052640 |
Adeno-associated virus serotype 9 containing CRISPR/Cas13Y and guide RNA against the human MECP2 gene
|
|
Current
|
| 300000038205 |
Adeno-associated virus serotype 9 containing human MYBPC3 gene
|
|
Current
|
| 300000013420 |
Adeno-associated virus serotype 9 containing the human ASPA gene
|
|
Current
|
| 300000046824 |
Adeno-associated virus serotype 9 containing the human RPE65 gene
|
|
Current
|
| 300000019872 |
Adeno-associated virus serotype 9 encoding human SMN
|
|
Current
|
| 300000046694 |
Adeno-associated virus serotype 9 expressing a transcription factor for the SCN1A gene
|
|
Current
|
| 300000026633 |
Adeno-associated virus serotype 9 expressing human CLN5
|
|
Current
|
| 300000028291 |
Adeno-associated virus serotype 9 expressing the cDNA for human MECP2
|
|
Current
|
| 300000037638 |
Adeno-associated virus serotype 9 expressing the human fukutin related protein and target sequence of the miR-208a
|
|
Current
|
| 100000183901 |
ADENO-ASSOCIATED VIRUS SEROTYPE 9 VECTOR CONTAINING HUMAN N-ACETYLGALACTOSAMINE-6-SULFATE SULFATASE GENE
|
|
Current
|
| 300000049893 |
Adeno-associated virus serotype 9 vector containing the human LAMP2 isoform B transgene
|
|
Current
|
| 300000032884 |
Adeno-associated virus serotype 9 encoding human NGLY1 gene
|
|
Current
|
| 300000052178 |
Adeno-associated virus serotype A101 containing the codon-optimized human CFTRdeltaR
|
|
Current
|
| 300000039586 |
Adeno-associated virus serotype C102 containing the human GLA gene
|
|
Current
|
| 300000039046 |
Adeno-associated virus serotype HSC 15 expressing human iduronate 2-sulfatase
|
|
Current
|
